Bringing together global mouse resources for a start-to-finish approach to model development.
JAX Professor Robert Burgess and collaborators are developing personalized gene therapy for a Texas child suffering from a neuromuscular disease.
Cortney Lavorgna is a college student who is exploring the neuromuscular disease she lives with in a JAX research experience.
Neuromuscular diseases start by hampering mobility and progress to threatening vital processes like breathing and swallowing. Greg Cox wants to knock them all out.
For the rarest of rare genetic conditions, a one-of-a-kind mouse could light a path to new treatments.